| Year |
Citation |
Score |
| 2023 |
Ferla R, Dell'Aquila F, Doria M, Ferraiuolo M, Noto A, Grazioli F, Ammendola V, Testa F, Melillo P, Iodice C, Risca G, Tedesco N, le Brun PR, Surace EM, Simonelli F, et al. Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B. Molecular Therapy. Methods & Clinical Development. 28: 396-411. PMID 36910588 DOI: 10.1016/j.omtm.2023.02.002 |
0.396 |
|
| 2022 |
Tornabene P, Ferla R, Llado-Santaeularia M, Centrulo M, Dell'Anno M, Esposito F, Marrocco E, Pone E, Minopoli R, Iodice C, Nusco E, Rossi S, Lyubenova H, Manfredi A, Di Filippo L, ... ... Surace EM, et al. Therapeutic homology-independent targeted integration in retina and liver. Nature Communications. 13: 1963. PMID 35414130 DOI: 10.1038/s41467-022-29550-8 |
0.393 |
|
| 2021 |
Tornabene P, Trapani I, Centrulo M, Marrocco E, Minopoli R, Lupo M, Iodice C, Gesualdo C, Simonelli F, Surace EM, Auricchio A. Inclusion of a degron reduces levelsof undesired inteins after AAV-mediated proteinsplicing in the retina. Molecular Therapy. Methods & Clinical Development. 23: 448-459. PMID 34786437 DOI: 10.1016/j.omtm.2021.10.004 |
0.393 |
|
| 2021 |
Marrocco E, Maritato R, Botta S, Esposito M, Surace EM. Challenging Safety and Efficacy of Retinal Gene Therapies by Retinogenesis. International Journal of Molecular Sciences. 22. PMID 34071252 DOI: 10.3390/ijms22115767 |
0.493 |
|
| 2021 |
Patrizi C, Llado M, Benati D, Iodice C, Marrocco E, Guarascio R, Surace EM, Cheetham ME, Auricchio A, Recchia A. Allele-specific editing ameliorates dominant retinitis pigmentosa in a transgenic mouse model. American Journal of Human Genetics. 108: 295-308. PMID 33508235 DOI: 10.1016/j.ajhg.2021.01.006 |
0.44 |
|
| 2020 |
Reynaud-Dulaurier R, Benegiamo G, Marrocco E, Al-Tannir R, Surace EM, Auwerx J, Decressac M. Gene replacement therapy provides benefit in an adult mouse model of Leigh syndrome. Brain : a Journal of Neurology. PMID 32413099 DOI: 10.1093/brain/awaa105 |
0.309 |
|
| 2019 |
Karali M, Guadagnino I, Marrocco E, De Cegli R, Carissimo A, Pizzo M, Casarosa S, Conte I, Surace EM, Banfi S. AAV-miR-204 Protects from Retinal Degeneration by Attenuation of Microglia Activation and Photoreceptor Cell Death. Molecular Therapy. Nucleic Acids. 19: 144-156. PMID 31837604 DOI: 10.1016/j.omtn.2019.11.005 |
0.307 |
|
| 2019 |
Tornabene P, Trapani I, Minopoli R, Centrulo M, Lupo M, de Simone S, Tiberi P, Dell'Aquila F, Marrocco E, Iodice C, Iuliano A, Gesualdo C, Rossi S, Giaquinto L, Albert S, ... ... Surace EM, et al. Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina. Science Translational Medicine. 11. PMID 31092694 DOI: 10.1126/Scitranslmed.Aav4523 |
0.511 |
|
| 2017 |
Botta S, de Prisco N, Marrocco E, Renda M, Sofia M, Curion F, Bacci ML, Ventrella D, Wilson C, Gesualdo C, Rossi S, Simonelli F, Surace EM. Targeting and silencing of rhodopsin by ectopic expression of the transcription factor KLF15. Jci Insight. 2. PMID 29263295 DOI: 10.1172/jci.insight.96560 |
0.331 |
|
| 2015 |
Trapani I, Banfi S, Simonelli F, Surace EM, Auricchio A. Gene therapy of inherited retinal degenerations: prospects and challenges. Human Gene Therapy. 26: 193-200. PMID 25762209 DOI: 10.1089/Hum.2015.030 |
0.488 |
|
| 2013 |
Manfredi A, Marrocco E, Puppo A, Cesi G, Sommella A, Della Corte M, Rossi S, Giunti M, Craft CM, Bacci ML, Simonelli F, Surace EM, Auricchio A. Combined rod and cone transduction by adeno-associated virus 2/8. Human Gene Therapy. 24: 982-92. PMID 24067103 DOI: 10.1089/hum.2013.154 |
0.528 |
|
| 2013 |
Puppo A, Bello A, Manfredi A, Cesi G, Marrocco E, Della Corte M, Rossi S, Giunti M, Bacci ML, Simonelli F, Surace EM, Kobinger GP, Auricchio A. Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina. Plos One. 8: e59025. PMID 23520549 DOI: 10.1371/Journal.Pone.0059025 |
0.553 |
|
| 2013 |
Testa F, Maguire AM, Rossi S, Pierce EA, Melillo P, Marshall K, Banfi S, Surace EM, Sun J, Acerra C, Wright JF, Wellman J, High KA, Auricchio A, Bennett J, et al. Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2. Ophthalmology. 120: 1283-91. PMID 23474247 DOI: 10.1016/J.Ophtha.2012.11.048 |
0.528 |
|
| 2012 |
Testa F, Rossi S, Sodi A, Passerini I, Di Iorio V, Della Corte M, Banfi S, Surace EM, Menchini U, Auricchio A, Simonelli F. Correlation between photoreceptor layer integrity and visual function in patients with Stargardt disease: implications for gene therapy. Investigative Ophthalmology & Visual Science. 53: 4409-15. PMID 22661472 DOI: 10.1167/Iovs.11-8201 |
0.414 |
|
| 2012 |
Rossi S, Testa F, Gargiulo A, Di Iorio V, Pierri RB, D'Alterio FM, Corte MD, Surace E, Simonelli F. The role of optical coherence tomography in an atypical case of oculocutaneous albinism: a case report. Case Reports in Ophthalmology. 3: 113-7. PMID 22548044 DOI: 10.1159/000337489 |
0.436 |
|
| 2012 |
Meola N, Pizzo M, Alfano G, Surace EM, Banfi S. The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retina. Rna (New York, N.Y.). 18: 111-23. PMID 22128341 DOI: 10.1261/rna.029454.111 |
0.341 |
|
| 2011 |
Karali M, Manfredi A, Puppo A, Marrocco E, Gargiulo A, Allocca M, Corte MD, Rossi S, Giunti M, Bacci ML, Simonelli F, Surace EM, Banfi S, Auricchio A. MicroRNA-restricted transgene expression in the retina. Plos One. 6: e22166. PMID 21818300 DOI: 10.1371/Journal.Pone.0022166 |
0.357 |
|
| 2011 |
Testa F, Surace EM, Rossi S, Marrocco E, Gargiulo A, Di Iorio V, Ziviello C, Nesti A, Fecarotta S, Bacci ML, Giunti M, Della Corte M, Banfi S, Auricchio A, Simonelli F. Evaluation of Italian patients with leber congenital amaurosis due to AIPL1 mutations highlights the potential applicability of gene therapy. Investigative Ophthalmology & Visual Science. 52: 5618-24. PMID 21474771 DOI: 10.1167/Iovs.10-6543 |
0.451 |
|
| 2011 |
Colella P, Iodice C, Di Vicino U, Annunziata I, Surace EM, Auricchio A. Non-erythropoietic erythropoietin derivatives protect from light-induced and genetic photoreceptor degeneration. Human Molecular Genetics. 20: 2251-62. PMID 21421996 DOI: 10.1093/Hmg/Ddr115 |
0.338 |
|
| 2011 |
Mussolino C, della Corte M, Rossi S, Viola F, Di Vicino U, Marrocco E, Neglia S, Doria M, Testa F, Giovannoni R, Crasta M, Giunti M, Villani E, Lavitrano M, Bacci ML, ... ... Surace EM, et al. AAV-mediated photoreceptor transduction of the pig cone-enriched retina. Gene Therapy. 18: 637-45. PMID 21412286 DOI: 10.1038/Gt.2011.3 |
0.637 |
|
| 2011 |
Mussolino C, Sanges D, Marrocco E, Bonetti C, Di Vicino U, Marigo V, Auricchio A, Meroni G, Surace EM. Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa. Embo Molecular Medicine. 3: 118-28. PMID 21268285 DOI: 10.1002/Emmm.201000119 |
0.332 |
|
| 2010 |
Simonelli F, Maguire AM, Testa F, Pierce EA, Mingozzi F, Bennicelli JL, Rossi S, Marshall K, Banfi S, Surace EM, Sun J, Redmond TM, Zhu X, Shindler KS, Ying GS, et al. Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. Molecular Therapy : the Journal of the American Society of Gene Therapy. 18: 643-50. PMID 19953081 DOI: 10.1038/Mt.2009.277 |
0.638 |
|
| 2010 |
Mussolino C, Bacci M, Simonelli F, Auricchio A, Surace E. Immunological, Toxicological and Biodistribution Studies in a Photoreceptor Targeting of Porcine Retina Journal of Biotechnology. 150: 468-468. DOI: 10.1016/J.Jbiotec.2010.09.695 |
0.319 |
|
| 2010 |
Mussolino C, Bacci M, Lavitrano M, Simonelli F, Auricchio A, Surace E. Study of Transduction Efficiencies of Three Vector Serotypes (AAV2/5, 2/7, 2/8) for Photoreceptor Targeting in Porcine Retina Journal of Biotechnology. 150: 467-467. DOI: 10.1016/J.Jbiotec.2010.09.693 |
0.38 |
|
| 2009 |
Maguire AM, High KA, Auricchio A, Wright JF, Pierce EA, Testa F, Mingozzi F, Bennicelli JL, Ying GS, Rossi S, Fulton A, Marshall KA, Banfi S, Chung DC, Morgan JI, ... ... Surace EM, et al. Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial. Lancet. 374: 1597-605. PMID 19854499 DOI: 10.1016/S0140-6736(09)61836-5 |
0.719 |
|
| 2009 |
Gargiulo A, Bonetti C, Montefusco S, Neglia S, Di Vicino U, Marrocco E, Corte MD, Domenici L, Auricchio A, Surace EM. AAV-mediated tyrosinase gene transfer restores melanogenesis and retinal function in a model of oculo-cutaneous albinism type I (OCA1). Molecular Therapy : the Journal of the American Society of Gene Therapy. 17: 1347-54. PMID 19436266 DOI: 10.1038/Mt.2009.112 |
0.499 |
|
| 2008 |
Maguire AM, Simonelli F, Pierce EA, Pugh EN, Mingozzi F, Bennicelli J, Banfi S, Marshall KA, Testa F, Surace EM, Rossi S, Lyubarsky A, Arruda VR, Konkle B, Stone E, et al. Safety and efficacy of gene transfer for Leber's congenital amaurosis. The New England Journal of Medicine. 358: 2240-8. PMID 18441370 DOI: 10.1056/Nejmoa0802315 |
0.634 |
|
| 2008 |
Surace EM, Auricchio A. Versatility of AAV vectors for retinal gene transfer. Vision Research. 48: 353-9. PMID 17923143 DOI: 10.1016/J.Visres.2007.07.027 |
0.544 |
|
| 2007 |
Allocca M, Mussolino C, Garcia-Hoyos M, Sanges D, Iodice C, Petrillo M, Vandenberghe LH, Wilson JM, Marigo V, Surace EM, Auricchio A. Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors. Journal of Virology. 81: 11372-80. PMID 17699581 DOI: 10.1128/Jvi.01327-07 |
0.733 |
|
| 2006 |
Surace EM, Balaggan KS, Tessitore A, Mussolino C, Cotugno G, Bonetti C, Vitale A, Ali RR, Auricchio A. Inhibition of ocular neovascularization by hedgehog blockade. Molecular Therapy : the Journal of the American Society of Gene Therapy. 13: 573-9. PMID 16343995 DOI: 10.1016/J.Ymthe.2005.10.010 |
0.384 |
|
| 2005 |
Rex TS, Peet JA, Surace EM, Calvert PD, Nikonov SS, Lyubarsky AL, Bendo E, Hughes T, Pugh EN, Bennett J. The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. Molecular Vision. 11: 1236-45. PMID 16402024 |
0.705 |
|
| 2005 |
Surace EM, Domenici L, Cortese K, Cotugno G, Di Vicino U, Venturi C, Cellerino A, Marigo V, Tacchetti C, Ballabio A, Auricchio A. Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer. Molecular Therapy : the Journal of the American Society of Gene Therapy. 12: 652-8. PMID 16023414 DOI: 10.1016/J.Ymthe.2005.06.001 |
0.525 |
|
| 2004 |
Rex TS, Allocca M, Domenici L, Surace EM, Maguire AM, Lyubarsky A, Cellerino A, Bennett J, Auricchio A. Systemic but not intraocular Epo gene transfer protects the retina from light-and genetic-induced degeneration. Molecular Therapy : the Journal of the American Society of Gene Therapy. 10: 855-61. PMID 15509503 DOI: 10.1016/J.Ymthe.2004.07.027 |
0.76 |
|
| 2004 |
Dejneka NS, Surace EM, Aleman TS, Cideciyan AV, Lyubarsky A, Savchenko A, Redmond TM, Tang W, Wei Z, Rex TS, Glover E, Maguire AM, Pugh EN, Jacobson SG, Bennett J. In utero gene therapy rescues vision in a murine model of congenital blindness. Molecular Therapy : the Journal of the American Society of Gene Therapy. 9: 182-8. PMID 14759802 DOI: 10.1016/J.Ymthe.2003.11.013 |
0.755 |
|
| 2004 |
Surace EM, Auricchio A. Corrigendum to “Adeno-associated viral vectors for retinal gene transfer” [Progress in Retinal and Eye Research 22 (2003) 705–719] Progress in Retinal and Eye Research. 23: 251. DOI: 10.1016/J.Preteyeres.2003.11.001 |
0.516 |
|
| 2003 |
Liang FQ, Surace E, Dejneka NS, Maguire AM, Bennett J. Müller cell transduction by AAV2 in normal and degenerative retinas. Advances in Experimental Medicine and Biology. 533: 439-45. PMID 15180296 DOI: 10.1007/978-1-4615-0067-4_56 |
0.648 |
|
| 2003 |
Dejneka NS, Surace EM, Bennett J. Gene therapy for Leber congenital amaurosis. Advances in Experimental Medicine and Biology. 533: 415-22. PMID 15180293 DOI: 10.1007/978-1-4615-0067-4_53 |
0.757 |
|
| 2003 |
Surace EM, Auricchio A. Adeno-associated viral vectors for retinal gene transfer. Progress in Retinal and Eye Research. 22: 705-19. PMID 14575721 DOI: 10.1016/S1350-9462(03)00052-1 |
0.501 |
|
| 2003 |
Surace EM, Auricchio A, Reich SJ, Rex T, Glover E, Pineles S, Tang W, O'Connor E, Lyubarsky A, Savchenko A, Pugh EN, Maguire AM, Wilson JM, Bennett J. Delivery of adeno-associated virus vectors to the fetal retina: impact of viral capsid proteins on retinal neuronal progenitor transduction. Journal of Virology. 77: 7957-63. PMID 12829835 DOI: 10.1128/Jvi.77.14.7957-7963.2003 |
0.776 |
|
| 2002 |
Behling KC, Surace EM, Bennett J. Pigment epithelium-derived factor expression in the developing mouse eye. Molecular Vision. 8: 449-54. PMID 12447163 |
0.734 |
|
| 2002 |
Ho TT, Maguire AM, Aguirre GD, Surace EM, Anand V, Zeng Y, Salvetti A, Hopwood JJ, Haskins ME, Bennett J. Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VI. The Journal of Gene Medicine. 4: 613-21. PMID 12439853 DOI: 10.1002/Jgm.302 |
0.675 |
|
| 2001 |
Karakousis PC, John SK, Behling KC, Surace EM, Smith JE, Hendrickson A, Tang WX, Bennett J, Milam AH. Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues. Molecular Vision. 7: 154-63. PMID 11438800 |
0.733 |
|
| 2000 |
Surace EM, Angeletti B, Ballabio A, Marigo V. Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium. Investigative Ophthalmology & Visual Science. 41: 4333-7. PMID 11095635 |
0.377 |
|
| 2000 |
Incerti B, Cortese K, Pizzigoni A, Surace EM, Varani S, Coppola M, Jeffery G, Seeliger M, Jaissle G, Bennett DC, Marigo V, Schiaffino MV, Tacchetti C, Ballabio A. Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1. Human Molecular Genetics. 9: 2781-8. PMID 11092754 DOI: 10.1093/Hmg/9.19.2781 |
0.351 |
|
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