Year |
Citation |
Score |
2022 |
Smith MC, Belur LR, Karlen AD, Erlanson O, Podetz-Pedersen KM, McKenzie J, Detellis J, Gagnidze K, Parsons G, Robinson N, Labarre S, Shah S, Furcich J, Lund T, Tsai HC, et al. Phenotypic correction of murine mucopolysaccharidosis type II by engraftment of lentiviral vector transduced hematopoietic stem and progenitor cells. Human Gene Therapy. PMID 36226412 DOI: 10.1089/hum.2022.141 |
0.474 |
|
2020 |
Belur LR, Podetz-Pedersen KM, Tran TA, Mesick JA, Singh NM, Riedl M, Vulchanova L, Kozarsky KF, McIvor RS. Intravenous delivery for treatment of mucopolysaccharidosis type I: A comparison of AAV serotypes 9 and rh10. Molecular Genetics and Metabolism Reports. 24: 100604. PMID 32461912 DOI: 10.1016/J.Ymgmr.2020.100604 |
0.591 |
|
2017 |
Belur LR, Temme A, Podetz-Pedersen KM, Riedl M, Vulchanova L, Robinson N, Hanson LR, Kozarsky KF, Orchard PJ, Frey Ii WH, Low WC, McIvor RS. Intranasal AAV Mediated Gene Delivery and Expression of Human Iduronidase in the CNS: A Non-invasive and Effective Approach for Prevention of Neurologic Disease in Mucopolysaccharidosis Type I. Human Gene Therapy. PMID 28462595 DOI: 10.1089/Hum.2017.187 |
0.663 |
|
2014 |
Janson CG, Romanova LG, Leone P, Nan Z, Belur L, McIvor RS, Low WC. Comparison of Endovascular and Intraventricular Gene Therapy With Adeno-Associated Virus-α-L-Iduronidase for Hurler Disease. Neurosurgery. 74: 99-111. PMID 24077583 DOI: 10.1227/NEU.0000000000000157 |
0.329 |
|
2011 |
Wolf DA, Lenander AW, Nan Z, Belur LR, Whitley CB, Gupta P, Low WC, McIvor RS. Direct gene transfer to the CNS prevents emergence of neurologic disease in a murine model of mucopolysaccharidosis type I. Neurobiology of Disease. 43: 123-33. PMID 21397026 DOI: 10.1016/J.Nbd.2011.02.015 |
0.53 |
|
2009 |
Aronovich EL, Bell JB, Khan SA, Belur LR, Gunther R, Koniar B, Schachern PA, Parker JB, Carlson CS, Whitley CB, McIvor RS, Gupta P, Hackett PB. Systemic correction of storage disease in MPS I NOD/SCID mice using the sleeping beauty transposon system. Molecular Therapy : the Journal of the American Society of Gene Therapy. 17: 1136-44. PMID 19384290 DOI: 10.1038/Mt.2009.87 |
0.445 |
|
2008 |
Belur LR, McIvor RS, Wilber A. Liver-directed gene therapy using the sleeping beauty transposon system. Methods in Molecular Biology (Clifton, N.J.). 434: 267-76. PMID 18470650 DOI: 10.1007/978-1-60327-248-3_16 |
0.309 |
|
2007 |
Bell JB, Podetz-Pedersen KM, Aronovich EL, Belur LR, McIvor RS, Hackett PB. Preferential delivery of the Sleeping Beauty transposon system to livers of mice by hydrodynamic injection. Nature Protocols. 2: 3153-65. PMID 18079715 DOI: 10.1038/Nprot.2007.471 |
0.317 |
|
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