Year |
Citation |
Score |
2020 |
McCurdy VJ, Johnson AK, Gray-Edwards HL, Randle AN, Bradbury AM, Morrison NE, Hwang M, Baker HJ, Cox NR, Sena-Esteves M, Martin DR. Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease. Gene Therapy. PMID 32884151 DOI: 10.1038/S41434-020-00190-1 |
0.35 |
|
2017 |
Gray-Edwards H, Randle AN, Maitland S, Benatti H, Hubbard S, Canning P, Vogel M, Brunson B, Hwang M, Ellis L, Bradbury AM, Gentry A, Taylor A, Wooldridge A, Wilhite D, ... ... Cox NR, et al. AAV gene therapy in a sheep model of Tay-Sachs disease. Human Gene Therapy. PMID 28922945 DOI: 10.1089/Hum.2017.163 |
0.3 |
|
2017 |
Gray-Edwards HL, Regier DS, Shirley JL, Randle AN, Salibi N, Thomas SE, Latour YL, Johnston J, Golas G, Maguire AS, Taylor AR, Sorjonen DC, McCurdy VJ, Christopherson PW, Bradbury AM, ... ... Cox NR, et al. Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model. Molecular Therapy : the Journal of the American Society of Gene Therapy. PMID 28236574 DOI: 10.1016/J.Ymthe.2017.01.009 |
0.342 |
|
2016 |
Bradbury AM, Peterson TA, Gross AL, Wells SZ, McCurdy VJ, Wolfe KG, Dennis JC, Brunson BL, Gray-Edwards H, Randle AN, Johnson AK, Morrison EE, Cox NR, Baker HJ, Sena-Esteves M, et al. AAV Mediated Gene Delivery Attenuates Neuroinflammation in Feline Sandhoff Disease. Neuroscience. PMID 27793778 DOI: 10.1016/J.Neuroscience.2016.10.047 |
0.332 |
|
2015 |
Gray-Edwards HL, Brunson BL, Holland M, Hespel AM, Bradbury AM, McCurdy VJ, Beadlescomb PM, Randle AN, Salibi N, Denney TS, Beyers RJ, Johnson AK, Voyles ML, Montgomery RD, Wilson DU, ... ... Cox NR, et al. Mucopolysaccharidosis-like phenotype in feline Sandhoff disease and partial correction after AAV gene therapy. Molecular Genetics and Metabolism. PMID 25971245 DOI: 10.1016/J.Ymgme.2015.05.003 |
0.354 |
|
2015 |
Rockwell HE, McCurdy VJ, Eaton SC, Wilson DU, Johnson AK, Randle AN, Bradbury AM, Gray-Edwards HL, Baker HJ, Hudson JA, Cox NR, Sena-Esteves M, Seyfried TN, Martin DR. AAV-mediated gene delivery in a feline model of Sandhoff disease corrects lysosomal storage in the central nervous system. Asn Neuro. 7. PMID 25873306 DOI: 10.1177/1759091415569908 |
0.358 |
|
2015 |
McCurdy VJ, Rockwell HE, Arthur JR, Bradbury AM, Johnson AK, Randle AN, Brunson BL, Hwang M, Gray-Edwards HL, Morrison NE, Johnson JA, Baker HJ, Cox NR, Seyfried TN, Sena-Esteves M, et al. Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease. Gene Therapy. 22: 181-9. PMID 25474439 DOI: 10.1038/Gt.2014.108 |
0.363 |
|
2015 |
Bradbury AM, Gray-Edwards HL, Shirley JL, McCurdy VJ, Colaco AN, Randle AN, Christopherson PW, Bird AC, Johnson AK, Wilson DU, Hudson JA, De Pompa NL, Sorjonen DC, Brunson BL, Jeyakumar M, ... ... Cox NR, et al. Biomarkers for disease progression and AAV therapeutic efficacy in feline Sandhoff disease. Experimental Neurology. 263: 102-12. PMID 25284324 DOI: 10.1016/J.Expneurol.2014.09.020 |
0.344 |
|
2014 |
McCurdy VJ, Johnson AK, Gray-Edwards HL, Randle AN, Brunson BL, Morrison NE, Salibi N, Johnson JA, Hwang M, Beyers RJ, Leroy SG, Maitland S, Denney TS, Cox NR, Baker HJ, et al. Sustained normalization of neurological disease after intracranial gene therapy in a feline model. Science Translational Medicine. 6: 231ra48. PMID 24718858 DOI: 10.1126/Scitranslmed.3007733 |
0.348 |
|
2013 |
Bradbury AM, Cochran JN, McCurdy VJ, Johnson AK, Brunson BL, Gray-Edwards H, Leroy SG, Hwang M, Randle AN, Jackson LS, Morrison NE, Baek RC, Seyfried TN, Cheng SH, Cox NR, et al. Therapeutic response in feline sandhoff disease despite immunity to intracranial gene therapy. Molecular Therapy : the Journal of the American Society of Gene Therapy. 21: 1306-15. PMID 23689599 DOI: 10.1038/Mt.2013.86 |
0.335 |
|
2009 |
Baek RC, Martin DR, Cox NR, Seyfried TN. Comparative analysis of brain lipids in mice, cats, and humans with Sandhoff disease. Lipids. 44: 197-205. PMID 19034545 DOI: 10.1007/S11745-008-3268-0 |
0.3 |
|
2007 |
Wang L, Martin DR, Baker HJ, Zinn KR, Kappes JC, Ding H, Gentry AS, Harper S, Snyder EY, Cox NR. Neural progenitor cell transplantation and imaging in a large animal model. Neuroscience Research. 59: 327-40. PMID 17897743 DOI: 10.1016/J.Neures.2007.08.011 |
0.304 |
|
2006 |
Martin DR, Cachon-Gonzalez B, Sena- Esteves M, Hwang M, Gentry AS, Morrison NE, Cox NR, Cox TM, Baker HJ. 889. Adeno-Associated Virus Gene Therapy of Feline Gangliosidosis Molecular Therapy. 13: S342. DOI: 10.1016/J.Ymthe.2006.08.978 |
0.337 |
|
2005 |
Martin DR, Haack K, Niemeyer GP, Cox NR, Kafri T, Baker HJ. 962. Treatment of Feline GM1 Gangliosidosis with Mesenchymal Stem Cells and Lentiviral Gene Therapy Molecular Therapy. 11. DOI: 10.1016/J.Ymthe.2005.07.505 |
0.344 |
|
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